common.study.topics.clinical

Testing Experimental Treatment for Frontotemporal Dementia

common.study.values.description

“A Study to Evaluate Safety of Long-term AL001 Dosing in FTD Patients”

A Phase 2 open label study evaluating the safety, tolerability, PK and PD of AL001 in participants with a Granulin mutation or C9orf72 mutation causative of frontotemporal dementia.

common.study.values.location

participant.ui.study.affiliations-map.online-study.header-virtual

participant.ui.study.affiliations-map.online-study.text

participant.ui.study.affiliations-map.legend.locations participant.ui.study.affiliations-map.legend.selected

common.study.values.methods

Pharmaceutical medication involved common.study.methods.has-drugs-yes
Recruiting patients only common.study.methods.is-healthy-yes

Drug - AL001

administered via intravenous (IV) infusion once a month

participant.views.study.view.additional

participant.views.study.view.scientific-title

A Phase 2, Multicenter, Open-Label Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of AL001 in Heterozygous Carriers of Granulin or C9ORF72 Mutations Causative of Frontotemporal Dementia

common.study.values.clinical-trial-id

NCT03987295

participant.views.study.view.id

bYE92b