Testing Experimental Frontotemporal Dementia Medication
common.study.values.description
“A First in Human Study in Healthy Volunteers and in Participants With Frontotemporal Dementia With Granulin Mutation”
A first in human phase 1 study in healthy volunteers and participants with Granulin mutation causative of frontotemporal dementia (FTD) to assess AL001 safety, tolerability, pharmacokinetics, and pharmacodynamics
common.study.values.location
participant.ui.study.affiliations-map.online-study.header-virtual
participant.ui.study.affiliations-map.online-study.text
common.study.values.methods


Biological - AL001
Active dose of AL001
Placebo
Saline solution administered as a single infusion as palcebo.
participant.views.study.view.additional
participant.views.study.view.scientific-title
A First in Human Phase 1 Study in Healthy Volunteers and in Participants With Frontotemporal Dementia (FTD) With Granulin Mutation
common.study.values.clinical-trial-id
NCT03636204
participant.views.study.view.id
bkRZNa